ProQR Therapeutics We strive to reverse blindness

Living with Inherited retinal disease - Maartje de Kok and her family

Our programs

Rare Disease Day 2021

We are excited to support Rare Disease Day 2021 on February 28th. On this day we raise awareness around rare diseases and in particular rare blinding disorders known as inherited retinal diseases, or IRDs. Although IRDs are rare, when combined over 2 million people worldwide experience vision loss because of one. Most IRDs currently have no treatment options available and it's ProQR's mission to change that.

Read more about IRDs
ProQR supports Rare Disease Day, 28 February 2021 - rare is many, rare is strong, rare is proud

Stories that inspire our work

  • Life around the diagnosis with Leber congenital amaurosis

    Laura Steinbusch has a son, 5-year-old Enzo, who has been diagnosed with Leber congenital amaurosis 10, or LCA10. It has made Laura a patient advocate for this disease, and in this interview she explains how the diagnosis has changed her life.

    • Leber congenital amaurosis
    • Genetic testing
    • Blindness
    • Story
    Photo of Laura Steinbusch and family

  • In it for the patient

    The ProQR family is growing fast and we spoke to the Chief Medical Officer Aniz Girach who joined ProQR in 2019. We asked him about his impression of the company after he joined, as well as the new developments he’s been working on.

    • Programs general
    • Sepofarsen (QR-110)
    • IRD general
    • pipeline
    • Clinical trial
    A photo of Aniz Girach

  • Serving a tight-knit community

    The Netherlands boasts the most prominent patient organization for Usher syndrome. Part of their secret is the passion of the Board. We caught up with president Ivonne Bressers and the Board’s secretary Annouk van Nunen at Annouk’s home in Leiden.

    • QR-421a
    • Usher syndrome
    • patient advocacy
    • Genetic testing
    • Story
    Photo of Annouk van Nunen and Ivonne Bressers

Patient-focused drug development

We are a biotechnology company dedicated to changing lives. Our focus lies with developing RNA therapies to reverse vision loss for people living with inherited retinal disease (IRD). From day one we have put patients first and we continue striving to incorporate their voice at every step of drug-development. We believe this patient-focused approach is crucial to our success.

For the IRD community
A photo of Cristian, Silvia and their kids Edoardo and Beatrice. Beatrice has Lber congenital amaurosis 10

Latest press releases

More press releases
Female scientist working in the lab

Free genetic testing now available

ProQR has teamed up with the Foundation Fighting Blindness to provide no-cost genetic testing to inherited retinal disease patients in the United States. Learn how the My Retina Tracker program empowers the US IRD community and helps research into new treatments.

Learn about My Retina Tracker
My Retina Tracker logo

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