Blogs, Stories & News

  • Always excited about RNA therapies

    He is one of the founders of ProQR, but even long before that Gerard Platenburg was involved in the development of RNA therapies. Even so, after decades of working on them he still gets enthusiastic when talking about RNA.

    • RNA therapies
    • innovation
    • Research
    A photo of Gerard Platenburg
  • Still going strong / One challenge after another

    There are currently around 160 people working at ProQR, but that wasn’t always the case. When Hee Lam Chan joined in 2013, she was only employee number six. As a result, she has seen the company grow and develop.

    • Ophthalmology
    • organoids
    • pipeline
    • innovation
    A photo of Hee Lam Chan
  • Life around the diagnosis with Leber congenital amaurosis

    Laura Steinbusch has a son, 5-year-old Enzo, who has been diagnosed with Leber congenital amaurosis 10, or LCA10. It has made Laura a patient advocate for this disease, and in this interview she explains how the diagnosis has changed her life.

    • Leber congenital amaurosis
    • Genetic testing
    • Blindness
    • Story
    Photo of Laura Steinbusch and family
  • Serving a tight-knit community

    The Netherlands boasts the most prominent patient organization for Usher syndrome. Part of their secret is the passion of the Board. We caught up with president Ivonne Bressers and the Board’s secretary Annouk van Nunen at Annouk’s home in Leiden.

    • QR-421a
    • Usher syndrome
    • patient advocacy
    • Genetic testing
    • Story
    Photo of Annouk van Nunen and Ivonne Bressers
  • Data from InSight, an extension trial for Leber congenital amaurosis 10

    During a ProQR Expert Perspective call Dr. Girach (CMO at ProQR) discusses findings from an open label extension study of sepofarsen for LCA10 with Retinal Disease expert Dr. MacDonald (Prof Emer University of Alberta).

    • Sepofarsen (QR-110)
    • Leber congenital amaurosis
    • Clinical trial
    • Research
    On the left-hand sight a face picture of Dr. Ian MacDonald and on the right-hand side a face picture of Dr. Aniz Girach.
  • Why is the patient perspective in research important?

    Podcast on how the patient's perspective can positively impact research from protocol development to clinical trials. Featuring Francesca (information specialist, living with Leber congenital amaurosis) and Laura (Fighting Blindness Ireland).

    • IRD general
    • ProQR Talks podcast
    • Research and development
    • Leber congenital amaurosis
    ProQR Talks