ProQR is dedicated to developing RNA therapies to improve the lives of patients, families and communities living with inherited retinal diseases, a group of rare diseases causing blindness. To achieve this goal, ProQR strives to integrate the patient voice into our decision-making throughout the drug development process as we believe that a patient-focused strategy is crucial to our success.
Check out our blog that features patient stories, interviews, podcast episodes, program updates and more.
See all blog posts
If you have questions or want to stay informed please contact patientinfo@proqr.com or sign up for our Eye Connect newsletter.
Inherited retinal diseases (IRDs) are a group of rare genetic disorders that can cause severe vision loss or blindness, affecting around 2 million people worldwide.
Here is a list of all our ongoing clinical trials.
If you are not sure what a clinical trial is all about? Read this first.
Phase 2/3 clinical trial of sepofarsen for CEP290 mediated Leber congenital amaurosis (LCA10).
Phase 1/2 clinical trial of QR-421a for USH2A mediated retinitis pigmentosa and Usher syndrome.
Phase 1/2 clinical trial of QR-1123 for RHO mediated retinitis pigmentosa.
Learn how the latest RNA technologies can help treat rare genetic diseases
