… transformative RNA therapies based on its proprietary Axiomer ™ RNA editing technology platform, today reported its … at the RNA Editing Summit in Boston, highlighting its Axiomer technology platform and AX-0810, the Company’s … with meaningful changes in biomarkers in NHPs using Axiomer RNA Editing Oligonucleotides. At ASGCT, ProQR and …
… transformative RNA therapies based on its proprietary Axiomer ™ RNA editing technology platform today announced … will then be available for approximately 30 days. About Axiomer ™ ProQR is pioneering a next-generation RNA base editing technology called Axiomer ™ , which could potentially yield a new class of …
… Our leading intellectual property portfolio protects our Axiomer ® ADAR-mediated RNA editing platform technology and … patent protection related to its RNA editing platform, Axiomer ® , including more than 11 published patent families, … its IP estate around ADAR-mediated RNA editing. About Axiomer ® ProQR is pioneering a next-generation RNA base …
… transformative RNA therapies based on its proprietary Axiomer ® RNA editing technology platform, today reported its … pleased with the continued progress in advancing our Axiomer ® RNA editing platform and believe we’re only at the … In November ProQR announced its IP estate surrounding its Axiomer ® RNA editing platform was further strengthened by: …
Advancing AX-0810 through ongoing Phase 1 dosing, with target engagement data expected 1H 2026Selected Development Candidates AX-2402 for Rett syndrome (MECP2, R270X) and AX-2911 for MASH (PNPLA3)Ended 2025 with € 92.4 million cash and cash equivalents and achie
Initial AX-0810 data show no safety signals after 4 weeks of dosing and pharmacokinetics consistent with non-clinical data; Phase 1 enrollment and dosing in healthy volunteers ongoing with target engagement data expected in H1 2026, followed by inclusion of a patient cohort
… Announces Year End 2024 Operating and Financial Results Axiomer™ ADAR-mediated RNA editing pipeline advancing across … transformative RNA therapies based on its proprietary Axiomer RNA editing technology platform, today reported its …
… targeting NTCP for cholestatic diseases to be first ProQR Axiomer™ RNA editing program to enter the clinic Company to … at our Investor and Analyst Event in December. With our Axiomer™ RNA editing platform, a differentiated pipeline, a …