… Top-Line Results from Phase 2/3 Illuminate Trial of Sepofarsen in CEP290-mediated LCA10 Study did not meet … 12. “Given the results observed in earlier studies of sepofarsen, the Illuminate trial results are unexpected and …
Agreement provides ProQR with initial payment of €12.5M and up to €135M in further payments, as well as potential additional earn outs based on commercial sales in the US and EU
Divestment of sepofarsen and ultevursen supports ProQR’s strategic focus on the Axiomer®&
Top-line results expected H1 2022
Sepofarsen is a potential first-in-class RNA therapy for the treatment of LCA10, a rare inherited retinal disorder that leads to blindness
LEIDEN, Netherlands & CAMBRIDGE, Mass., Jan.
… ProQR Announces Virtual Presentation of Phase 1/2 Sepofarsen Extension Trial Data at the Association for … from the Company’s Phase 1/2 InSight extension trial of sepofarsen and live Q&A session at the Association for …
… ProQR Announces Expert Perspectives Call on LCA10 and Sepofarsen Call on July 20 will include a snapshot from the ongoing InSight open-label extension study of sepofarsen, including preliminary second eye treatment data …
… Completed 12 Month Visit in Phase 2/3 Illuminate Trial of Sepofarsen Top-line data now expected to be announced in Q1 2022 Sepofarsen is a potential first-in-class RNA therapy for the …
… Positive Top-Line Results from the Phase 1/2 Study of Sepofarsen in LCA10 Patients Reported rapid, significant and … Illuminate, were more likely to respond to treatment with sepofarsen. Table: Change from baseline in treated eye …
… ProQR Announces Additional Sepofarsen Illuminate Trial Analyses and Provides Update on … will focus on the following core activities related to sepofarsen: In Q3, the Company plans to meet with the EMA and …
… ProQR Announces Virtual Presentation of Phase 1/2 Sepofarsen Data Through the Association for Research in … presentation of data from the Company’s Phase 1/2 trial of sepofarsen. The data will be shared via a video presentation …
ProQR will focus exclusively on the development of the Axiomer® RNA editing technology platform across multiple therapeutic areas. This comes following feedback from the European Medicines Agency (EMA) related to ProQR’s sepofarsen for Leber Congenital Amaurosis type 10 (LCA10).
