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  1. Results of a phase 1b/2 trial of intravitreal (IVT) sepofarsen (QR-110) antisense oligonucleotide in Leber congenital amaurosis 10 (LCA10) due to p.Cys998X mutation in the CEP290 gene

    ePoster

    … visual acuity, and full-field stimulus testing. Stephen R. Russell 1 , Arlene V. Drack 1 , Artur V. Cideciyan 2 , … Zaeytijd 3 , Aniz Girach 6 , Wil den Hollander 6 , Michael R. Schwartz 6 , David M. Rodman 6 1 Department of … Thomas Jefferson University, Philadelphia, PA, USA; 6 ProQR Therapeutics, Leiden, the Netherlands. Russell SR, …

    AAO 2020 poster - Sepofarsen clinical trial results for Leber congenital amaurosis 10

  2. Results of a phase 1b/2 trial of intravitreal (IVT) sepofarsen (QR-110) antisense oligonucleotide in Leber congenital amaurosis 10 (LCA10) due to p.Cys998X mutation in the CEP290 gene

    Presentation

    … visual acuity, and full-field stimulus testing. Stephen R. Russell 1 , Arlene V. Drack 1 , Artur V. Cideciyan 2 , … Zaeytijd 3 , Aniz Girach 6 , Wil den Hollander 6 , Michael R. Schwartz 6 , David M. Rodman 6 1 Department of … Thomas Jefferson University, Philadelphia, PA, USA; 6 ProQR Therapeutics, Leiden, the Netherlands. Video-recorded …

    ARVO 2020 - Sepofarsen phase 1b/2 clinical trial results for Leber congenital amaurosis 10