… highlights significant potential of ProQR’s Axiomer ® RNA base-editing platform and strengthens financial position … to changing lives through the creation of transformative RNA therapies for genetic eye diseases, today reported its … trial and is a first-in-class investigational RNAtherapy designed to address the underlying cause of Leber …
… to changing lives through the creation of transformative RNA therapies for genetic eye diseases, today reported its … and we are pleased to partner with them, aiming to bring a therapy to patients in an area of unmet need for a …
… to changing lives through the creation of transformative RNA therapies for severe genetic rare diseases, today … Phase 1b/2 trial results of intravitreal sepofarsen RNAtherapy in Leber congenital amaurosis 10 (LCA10) Presenter: …
… to changing lives through the creation of transformative RNA therapies for severe genetic rare diseases, today … Phase 1b/2 trial results of intravitreal sepofarsen RNAtherapy in Leber congenital amaurosis 10 (LCA10) Presenter: …
Call on July 20 will include a snapshot from the ongoing InSight open-label extension study of sepofarsen, including preliminary second eye treatment data
… in Q1 2022 Sepofarsen is a potential first-in-class RNAtherapy for the treatment of LCA10, a rare inherited retinal … to changing lives through the creation of transformative RNA therapies for genetic eye diseases today announced that …
… supports ProQR’s strategic focus on the Axiomer® RNA editing technology platform and continued advancement of … company dedicated to changing lives through transformative RNA therapies, and Laboratoires Théa, the leading independent … Sepofarsen Sepofarsen (QR-110) is an investigational RNAtherapy designed to restore vision in Leber congenital …
Top-line results expected H1 2022
Sepofarsen is a potential first-in-class RNA therapy for the treatment of LCA10, a rare inherited retinal disorder that leads to blindness
LEIDEN, Netherlands & CAMBRIDGE, Mass., Jan.
… ProQR to Focus Exclusively on Axiomer RNA-editing Technology and Partner Ophthalmology Programs In … to changing lives through the creation of transformative RNA therapies, today provided an update on its ophthalmology … s epofarsen Sepofarsen (QR-110) is an investigational RNAtherapy designed to restore vision in Leber congenital …