… Pipeline ProQR is pioneering a next-generation RNA technology called Axiomer™, which uses a cell’s own … clinical endpoints. Internal link ProQR pipeline RNAtherapy An RNAtherapy is designed to correct the …
… a rare genetic disorder, with the objective to develop RNA therapies for rare diseases. Prior to founding ProQR, … In 1992 Dr. Valerio was appointed professor of gene therapy at the University of Leiden, where he also received …
ProQR to host a conference call to discuss the top-line results of the Phase 2/3 Illuminate clinical trial of investigational RNA therapy sepofarsen in CEP20-mediated LCA10.
