Substantial progress in 2019 with final data from Phase 1/2 trial of sepofarsen for Leber’s congenital amaurosis 10 showing rapid, significant and durable improvements in vision; Phase 2/3 pivotal trial Illuminate initiated with data expected in H1 2021Phase 1/2 St
… an endogenously expressed RNA editing system called ADAR, which can direct the change of an Adenosine (A) to an Inosine (I) in the RNA – an Inosine is …
Top-line data from pivotal Phase 2/3 Illuminate trial of sepofarsen for CEP290-mediated LCA10 anticipated late Q1/early Q2 2022
Five-target collaboration with Lilly highlights significant potential of ProQR’s Axiomer® RNA base-editing pla
Phase 2/3 pivotal Illuminate trial of sepofarsen for LCA10 enrollment complete with top-line data anticipated in H1 2022
Positive data reported from the Phase 1/2 clinical trial of QR-421a for the treatment of Usher syndrome and non-syndromic retini
… ® , which uses a cell’s own editing machinery called ADAR (adenosine deaminase acting on RNA) to make specific … the risks, uncertainties and other factors in our filings made with the Securities and Exchange Commission, including …
… Axiomer®, which uses a cell’s own editing machinery called ADAR (adenosine deaminase acting on RNA) to make specific … the risks, uncertainties and other factors in our filings made with the Securities and Exchange Commission, including …
… Axiomer ® RNA editing technology platform and continued advancement of pipeline LEIDEN, Netherlands & CAMBRIDGE, … Officer of ProQR. “We look forward to continuing to advance our Axiomer RNA editing platform, with an initial … ® , which uses a cell’s own editing machinery called ADAR to make specific single nucleotide edits in RNA to …