… company was founded in 2012, our mission has been to help people living with rare diseases that currently have no treatment options. This remains an important focus of our company … Read more about our Founding story . Patient-focused drug development Patient-focused drug development In order to …
… pdf , 1.54 Mo Download link RNA Editing Summit (2024) Developing Axiomer RNA Editing Technology Towards Clinical Development pdf , 2.83 Mo Lien externe ASGCT (2024) … to Address Liver Originated Disorders Internal link OPT Congress (2023) Gerard Platenburg, Therapeutic potential …
… ways, including via the Whistleblower Hotline which is operated by a third party SpeakUp and always available. The … confidential communication, and also allows for (optional) anonymous reporting. Report submitted to the … who will decide on further steps of investigation, as appropriate. Whistleblower Hotline reports may be made via …
… was diagnosed with a rare disease, he started ProQR to develop RNA therapies for rare diseases. Before founding … background in RNA modulation and orphan drug discovery and development and is currently in charge of our R&D. Gerard has … has led in the development of structure-guided methods for optimizing chemically modified oligonucleotides for …
At ProQR, we are dedicated to improving the lives of patients and families affected by rare and common disorders using Axiomer, our innovative RNA editing platform technology.
At ProQR we take care to give all applicants a good experience and value their time and interest in applying to become a ProQRian. On this page, you can find an overview of what you can expect throughout the recruitment process, until your first onboarding week.
… sepofarsen captain. The work of her department, aimed at developing a novel drug for Leber congenital amaurosis 10 … in Venezuela and now heading ProQR’s LCA research and development team in Leiden (The Netherlands), has multiple reasons for being optimistic. Obviously, as a biotech scientist looking for a …
… simulations to support go/no-go decisions, trial design optimization, and regulatory interactions. Skills and … are a true believer of the value of a workforce in which people from diverse backgrounds are encouraged to develop themselves, personally and professionally. We believe …
… because it requires you to really attach yourself to one topic for four years, and that’s not my personality. I started looking at the Science Park here in Leiden for options. At the time ProQR was looking for five technicians, … that what works. The past year we have been working on optimizing protocols to grow cells from a patient’s skin into …
