… USA. In addition to our global presence, ProQR operates through a legal entity in China to support local … a difference in the lives of the communities we serve. Our proprietary Axiomer™ RNA editing technology platform enables … inform your health - but never limit it. Department: Development Location: Shanghai The Role: As Project Lead, IIT …
… ensuring that scientific data generated across Research & Development is structured, reliable, accessible, and … supporting researchers and cross-functional teams in adopting high-quality data standards throughout the data … with Research, Bioinformatics, IT, Quality, Clinical Development, and external partners, you will contribute to …
Submitted CTA for lead program AX-0810, targeting NTCP for cholestatic diseasesAdvancing AX-2402 program toward clinical candidate selection, targeting MECP2 (R270X) for Rett SyndromeHosting fall Analyst and Investor Event (virtual), featuring detailed AX-0810 P
Axiomer™ ADAR-mediated RNA editing pipeline advancing across liver and CNS programs, with CTA filing on track for Q2 2025 for lead program AX-0810 targeting NTCP for Cholestatic diseases Strengthened leadership with appointments of Chief Financial Officer and Chief
AX-0810 target engagement data in healthy volunteers on track for Q2 2026; biliary atresia selected as initial Phase 2 indicationPipeline expansion with advancement of AX-0811 (NTCP) and AX-0422 (IDUA) toward the clinic, supporting multiple upcoming clinical cataly