Community stories and news

In a Phase 1/2 clinical trial investigational RNA therapy QR-1123 showed target engagement. ProQR plans to start a Phase 2 study for RHO mediated retinitis pigmentosa.

In a guest blog the Foundation Fighting Blindness gives advice and what to do after receiving a diagnosis with an inherited retinal disease.

At ProQR we are getting ready for Usher Syndrome Awareness Day 2021 on September 18th. On this important day and during the month of September we will join the Usher community in raising awareness for this condition.

Mani grew up in Bombay, India but it wasn’t until he moved to the USA that he discovered he has Usher syndrome and got involved with the Usher Coalition.

For people with inherited sight loss in the UK the Unlock Genetics platform helps people understand the importance of genetic testing and how to access it.

This year we celebrate the tenth anniversary of Global Accessibility Awareness Day (GAAD), and we look back on the development of our own accessible website a year ago.

The clinical trial named Brighten evaluates the safety and tolerability of investigational RNA therapy sepofarsen in children with Leber congenital amaurosis.

A blog by Martin Hills from Retina UK living with Retinitis Pigmentosa on why research participation and genetic testing are essential in for drug development and how to get involved.

In a Phase 1/2 clinical trial investigational RNA therapy ultevursen (QR-421a) showed a benefit in vision. ProQR plans to start final phase trials for USH2A mediated retinitis pigmentosa.

ProQR played its part this year through personal interviews from ProQRians on what inspires them to develop RNA therapies for rare genetic diseases.

Our founder and CEO Daniel de Boer looks back at the challenges and successes of 2020 and discusses the milestones to look for in the upcoming year.

We caught up with Lance Johnson, a podcaster and video editor, living with autosomal dominant retinitis pigmentosa (adRP). Since moving to New York City, Lance has started the See-Through Podcast, championing people from across the disability communi