Community stories and news

  • “Top-notch science that leads to a treatment”

    Community news

    2017 may become a very exciting year for Patricia Biasutto, sepofarsen captain. The work of her department, aimed at developing a novel drug for Leber congenital amaurosis 10 (LCA10) patients, has progressed steadily. The team is expecting to start a first clinical trial in patients this year.

    A photo of Patricia Biasutto