ProQR will present new preclinical data for Axiomer, including the first preclinical data for its AX-0810 pipeline program for cholestatic diseases targeting NTCP at the ASGCT Annual Meeting, May 7-11, 2024, in Baltimore, Maryland.
He is one of the founders of ProQR, but even long before that Gerard Platenburg was involved in the development of RNA therapies. Even so, after decades of working on them he still gets enthusiastic when talking about RNA.
… Officer role, with leadership oversight of Axiomer ® RNA-editing platform technology John Maraganore, PhD, former … provide strategic oversight of ProQR’s proprietary Axiomer RNA-editing platform technology. He is the scientific … including further building out the Company’s Axiomer RNA-editing technology as a value-generating platform. Smital …
… (SAB). In vivo proof of concept data for novel Axiomer ® RNA editing platform technology presented at the OTS meeting … of concept data for its novel and proprietary Axiomer ® RNA editing technology platform at the Oligonucleotide …