… RNA therapy Find out how RNA therapy works, how it differs … underlying cause of the disease. Watch: How do ProQR's RNA therapies work? A short introduction to RNA therapies Why focus on RNA therapies? Why focus on RNA therapies? RNA therapies can …
ProQR is pioneering a next-generation RNA technology called Axiomer™, which uses a cell’s own editing machinery called ADAR to make specific single nucleotide edits in RNA to reverse a mutation or modulate protein expression and could potentially yield a new class of medicines for both rare and prevalent diseases with unmet need.
… a rare genetic disorder, with the objective to develop RNA therapies for rare diseases. Prior to founding ProQR, … Society and the Scientific Advisory Board of the Gene and RNA Therapy Center Tübingen, Germany. During his 25 years of … Society and the Scientific Advisory Board of the Gene and RNA Therapy Center Tübingen, Germany. During his 25 years of …
… company dedicated to changing lives by developing RNA therapies for severe rare and common diseases. We focus … and Cambridge, Massachusetts, USA. Learn more about RNA therapy and our Axiomer technology . We are on a mission …
ProQR to host a conference call to discuss the top-line results of the Phase 2/3 Illuminate clinical trial of investigational RNA therapy sepofarsen in CEP20-mediated LCA10.
