… RNA medicines for the treatment of severe genetic rare diseases, today announced upcoming presentations at the … cause loss of functional usherin protein that causes the disease. QR-421a is designed to exclude the genetic defect …
Presentation at the 18th International Symposium on Retinal Degeneration (RD2018) at 8:30 am GMT on Sept. 5th Investor conference call to be held at 8:15 am ET on Sept. 5th
… RNA medicines for the treatment of severe genetic rare diseases, today announced upcoming presentations at the … RNA medicines for the treatment of severe genetic rare diseases such as Leber’s congenital amaurosis 10 and …
ProQR receives exclusive worldwide license for IONIS-RHO-2.5Rx, now QR-1123, for autosomal dominant retinitis pigmentosa (adRP), a rare inherited form of blindness with no approved therapy