This presentation reviews Axiomer editing oligonucleotides (EONs) structure activity, the potential of Axiomer platform as well as its applicability for the treatment of liver originated disorders.
This is Gerard Platenburg's presentation at the 5th International Conference on Base Editing, Prime Editing & Related Enzymes (Deaminet 2024) in San Diego, California.
… and presented positive pre-clinical data at two European scientific conferences. WINGS, a Phase 1/2 safety and … F508del mutation were presented at the North American CF conference. A Phase 2 study is currently being designed and …
