ProQR Therapeutics We strive to reverse blindness

Living with Inherited retinal disease - Maartje de Kok and her family

Our programs

Lilly partnership announcement

We announced a global licensing and research collaboration with Eli Lilly and Company focused on the discovery, development, and commercialization of potential new medicines for genetic disorders in the liver and nervous system. The companies will use ProQR’s proprietary Axiomer® RNA editing platform to progress new drug targets toward clinical development and commercialization.

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An illustration of an ADAR enzyme (in white) attached to an RNA molecule (in green)

Featured blogs, stories and news

  • Global Usher Syndrome Awareness Day

    At ProQR we are getting ready for Usher Syndrome Awareness Day 2021 on September 18th. On this important day and during the month of September we will join the Usher community in raising awareness for this condition.

    • Ush Day
    • Usher syndrome
    • QR-421a
    Picture of Maartje with text: September is Usher syndrome awareness month. USH is a rare disease affecting hearing, balance and vision.

  • Retina UK: why genes matter

    For people with inherited sight loss in the UK the Unlock Genetics platform helps people understand the importance of genetic testing and how to access it.

    • Genetic Testing
    • IRD general
    Retina UK logo with text: Working for people with inherited sight loss

Patient-focused drug development

We are a biotechnology company dedicated to changing lives. Our focus lies with developing RNA therapies to reverse vision loss for people living with inherited retinal disease (IRD). From day one we have put patients first and we continue striving to incorporate their voice at every step of drug-development. We believe this patient-focused approach is crucial to our success.

For the IRD community
A photo of Cristian, Silvia and their kids Edoardo and Beatrice. Beatrice has Lber congenital amaurosis 10

Latest press releases

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Female scientist working in the lab

Free genetic testing now available

ProQR has teamed up with the Foundation Fighting Blindness to provide no-cost genetic testing to inherited retinal disease patients in the United States. Learn how the My Retina Tracker program empowers the US IRD community and helps research into new treatments.

Learn about My Retina Tracker
My Retina Tracker logo

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