In a Phase 1/2 clinical trial investigational RNA therapy QR-1123 showed target engagement. ProQR plans to start a Phase 2 study for RHO mediated retinitis pigmentosa.
At ProQR we are getting ready for Usher Syndrome Awareness Day 2021 on September 18th. On this important day and during the month of September we will join the Usher community in raising awareness for this condition.
Mani grew up in Bombay, India but it wasn’t until he moved to the USA that he discovered he has Usher syndrome and got involved with the Usher Coalition.
For people with inherited sight loss in the UK the Unlock Genetics platform helps people understand the importance of genetic testing and how to access it.
This year we celebrate the tenth anniversary of Global Accessibility Awareness Day (GAAD), and we look back on the development of our own accessible website a year ago.
